THE SCIENTIFIC ADVISORY BOARD MAINTAINS THE RESEARCH FOCUS ON TREATMENTS THAT CAN PROCEED FROM CLINIC TO PATIENTS AS SOON AS POSSIBLE

Dr. Joseph Gleeson, M.D.

Howard Hughes Medical Investigator, Residency Harvard Medical School, Chair: Rady Children’s Institute for Genomic Medicine

Dr. Arthur Horwich, M.D

Howard Hughes Medical Investigator, Sterling Professor of Genetics and Pediatrics, Yale School of Medicine, Lasker, CZI Breakthrough Prize

Head, Patricia and John Rosenwald Laboratory of Neurobiology & Genetics, Rockefeller University, Dean Graduate Program, Rockefeller

Ph.D., Rockefeller University, M.D., University of Geneva, Professor Faculty of Medicine, President University of Geneva (2007 to 2015)